Y-mAbs Therapeutics, Inc.

Q3 2023 Earnings Conference Call

11/14/2023

speaker
Operator
Good morning and welcome to YMAB's Therapeutics Third Quarter 2023 Earnings Conference Call. Please note that today's event is being recorded. At this time, all participants are in a listen-only mode. Instructions for the question and answer session will follow the prepared remarks. I would now like to turn the conference call over to Courtney Duggan, Vice President, Investor Relations. Please go ahead.
speaker
Courtney Duggan
Thank you, Operator, and good morning, everyone. Welcome to our third quarter 2023 earnings conference call. We issued a press release with our results yesterday at market close. The press release and accompanying slides are available on the investor relations section of our website. Let me quickly remind you that the following discussion contains certain statements that are considered forward-looking statements, as defined by the Private Securities Litigation Reform Act of 1995. Such statements include, but are not limited to, statements about our business model and development, commercialization and product distribution plans, expectations with respect to early trial data, current and future clinical and preclinical studies in our research and development programs, expectations related to the timing of the initiation and completion of regulatory submissions, regulatory marketing and reimbursement approvals, including statements with respect to future development of other development programs, potential for Danielle's and Territory expansion and advancement in SADA, collaborations or strategic partnerships and the potential benefits thereof, expectations related to our anticipated cash farm rights and the sufficiency of our cash resources and assumptions related thereto, guidance and expectations for 2023 and beyond, and our financial performance, including our estimates regarding revenues, expenses, and capital expenditure requirements, and other statements that are not historical facts. Because forward-looking statements involve risks and uncertainties, they are not guarantees of future potential performance, and actual results may differ materially from those expressed or implied by these forward-looking statements due to a variety of factors. including those risk factors discussed in the company's quarterly report on Form 10-Q for the quarter ended September 30th, 2023, as filed with the SEC on November 15th, 2023. I would now like to turn the call over to our founder, Vice Chairman of the Board of Directors, and Chief Business Officer, Thomas Gad.
speaker
Thomas Gad
Thank you, Courtney. Good morning, everybody, and thank you for joining us today. I have with me today our Chief Financial Officer, Bo Kruse, our Chief Commercial Officer, Sue Smith, and our Chief Scientific Officer, Dr. Stene Lispry. I'm also very excited to welcome our newly appointed President and Chief Executive Officer, Michael Rossi. On today's call, Mike will begin by reviewing third quarter global highlights on Danielsa sales, updates on our ongoing Nacitimab clinical trials, and high-level updates around our SADA program. Sue will then report further insights into our U.S. Danielsa sales in the third quarter. Next, Dean will provide further details on our Phase 1 DD2 SADA trial currently underway in addition to updates on our CD38 SADA program for which we recently received IND clearance by the U.S. FDA. Then Bo will provide an overview of our third quarter financial performance, our cash resources, and our full year 2023 guidance before we open the line for Q&A. Before we get into the third quarter results, on behalf of the YMAPS Board of Directors and our senior leadership team, I want to extend a very warm welcome to our new president and CEO, Michael Rossi, who officially started on November 6th. Our board has conducted a careful search for the right dedicated leader of our company with deep commercial and radiopharmaceutical experience. And we are very pleased to have found that in Mike. Michael brings over 30 years of experience in the radiopharmaceutical industry. He joins us from Merion Technologies, where he served as the president of the medical group. Prior to that, Mike was the head of radioligand imaging at Advanced Accelerator Applications, better known as AAA, a Novartis company. And before that, he led the growth of Jubilant Radiopharm into a vertical integrated radiopharmaceutical leader. Early on in his career, Mike spent over a decade at GE Healthcare, and he's also a certified nuclear pharmacist. As we continue our efforts to expand the geographic reach of Danielsa and further our indication expansion initiatives to maximize the utility of this therapy, we are also incredibly excited about our novel two-step pre-targeted radiotherapy platform, better known as SADA. and its potential to unlock the value of rated pharmaceuticals in the cancer treatment paradigm. After our reorg in the first quarter of this year, YMS has been positioned as one of the few independent commercial states biotech companies with sufficient financial resources to advance SADA through proof of concept. Is this the right time for me to transition to a new role of Vice Chairman and Chief Business Officer? And I very much look forward to working closely with Mike and our board and the entire YMAPS team on our continued mission to bring novel therapeutics to cancer patients. And with that, I'm very excited to turn the call over to Mike. Go ahead, Mike.
speaker
Courtney
Thank you, Thomas, for that introduction. It's great to be joining you all today for our YMAPS third quarter earnings call. As Thomas mentioned, I've built a 30-plus year career in healthcare with a specific focus on radiopharmaceuticals. YMAPS is a pioneer in pre-targeted radioimmune therapy with the SADA technology platform, which is a key driver of my own personal excitement about joining YMAPS. SADA stands out as a highly differentiated, pre-targeted, two-step platform that is designed to enable precise radioisotope delivery. I truly believe that SADA has the potential to shift the treatment paradigm in radiotherapy. In addition, we have the promising Daniela franchise, where we expect to have a growing stream of revenue with our commercial product to independently support our clinical development work with SADA in a rapidly expanding radiopharma market. With our Phase 1 GD2 SADA trial underway, and our Phase 1 CD38 SADA trial anticipated to initiate next year, and several additional exciting targets currently in preclinical development, we believe we have a highly promising clinical pipeline ahead.
speaker
Thomas
Now, let's dive into the key highlights for the quarter, starting with Danielza.
speaker
Courtney
As a reminder, Danielza is approved by the US FDA for the treatment of relapse or refractory high-risk neuroblastoma in the bone or bone marrow of patients who have demonstrated a partial response, minor response, or stable disease with prior therapies. Neuroblastoma is the most common cancer in infants and the third most common cancer in children. In the third quarter of this year, we achieved $20 million in net product sales of Danielza, up 59% from what we recorded in the third quarter of 2022. We continue to make significant progress in our commercialization efforts for Danielza, and we are gaining momentum in the U.S. with a number of new accounts. We now have 57 sites activated across the U.S. since Danielza's launch, with nine new accounts so far in 2023. We continue to expand our global commercial footprint through partnerships and recently received regulatory approval of Daniela in Mexico, marking our second regulatory approval in Latin America with our partner, Atom. In addition, or as discussed last quarter, our partner, Cyclone, successfully launched Daniela in China in June of this year. In terms of the number of vials used, in the first full quarter since the commercial launch in China, Usage in China has been approximately 50% of the vials used in the U.S. during the quarter. While it's still early, we look forward to seeing the sales progress and trends in the region over the coming months. We see China as a key region for Danielza, and we look forward to providing an update in the coming quarters. We continue to be very pleased with the WEP program in Europe, with 19 patients treated with Danielza through the end of Q3. The continued geographic expansion of Danielza across these regions is an important step in our mission to enable broad global access for Danielza for patients with high-risk relapsed refractory neuroblastoma. We remain encouraged by the expansion of Danielza, accumulating global net sales of more than $61 million in the first nine months of 2023 as we continue to gain further traction with physicians prescribing Danielza. We remain confident in our ability to continue to expand our global commercial market footprint and meet our full year 2023 Danielsa net product revenue guidance of between $80 and $85 million. Sue will provide further color on Danielsa sales in the quarter shortly.
speaker
Thomas
Now, let me briefly comment our ongoing Nexidimax clinical trials.
speaker
Courtney
We continue to make progress on our investment Gator sponsored clinical trials in collaboration with leading KOLs to efficiently advance potential label expansion opportunities for Danielsa. In the frontline high-risk neuroblastoma setting, we are partnering with the Beat Childhood Cancer Research Consortium, or BCC, in multi-center phase two trial, evaluating an Exidimab in combination with standard induction therapy for patients with newly diagnosed high risk neuroblastoma. To date, nine sites have been initiated and six patients have been dosed. The study is expected to transition from a single arm study with Nexidimab added to the current standard treatment for induction to a randomized study where the control arm will be the current standard of care for induction therapy, which is chemotherapy plus or minus an ALK inhibitor for which we plan to file an IMD. As a reminder, the patient recruitment for the trial is projected over a span of five years with an anticipated total trial sample size of approximately 282 patients. Our aim for the trial is to demonstrate a superiority in that minimum alarm versus standard of care. We expect to potentially initiate the new randomized study in the second quarter of next year. In osteosarcoma, we're continuing to work with Memorial Sloan Kettering Cancer Center, or MSK, on its multi-center investigator-censored trial for Nexidimab. We anticipate MSK to provide a data readout from this Phase I-II trial in the fourth quarter of 2024, and if positive, we hope to then begin our improvement for a pivotal randomized Phase III trial. In addition, we are pleased with the publication of the study of Exidimab-based chemoimmunotherapy hits trial in patients with chemo-resistant high-risk neuroblastoma in the journal cancers. In this trial, patients who received hits immediately after induction had a higher response rates, 47% versus 18%, and superior estimated three-year overall survival, 85% versus 29%, compared with those who received the same combination regimen later in the course of treatment. These results further supported the utilization of Nexidimab early during the course of treatment for patients with chemoresistant high-risk neuroblastoma. We are continuing to work to unlock further value of Nexidimab and truly believe in its potential to fill a much needed treatment gaps in both pediatric and adult cancers for patients worldwide. Now, moving on to SADA. Our novel SADA technology platform is a key driver of my own personal excitement about joining YMABS. Throughout my extensive career in various radiopharma leadership roles, I've had the privilege to witness the development of numerous breakthrough technological platforms. However, SADA, which is licensed by YMABS from MSK and the Massachusetts Institute of Technology in 2020, stands out as a highly differentiated, pre-targeted two-step platform that is designed to enable precise radioisotope delivery. We truly believe that SADA has the potential to shift the radiotherapy treatment paradigm and potentially be impactful in the fight against a wide variety of cancers. Steve will provide further color on our specific platforms later in today's call, but let me provide a high-level overview of where we currently are with our SADA pipeline. Our first program, GD2 SADA, began phase one development earlier this year. To date, we have completed dosing cohorts one and two, currently administering doses in cohort three. Despite the limited patient sample size to date, we're very pleased with the positive progress we've seen so far, and we have decided to share early PK and proof of concept for our SADA platform during this call. Due to the progress we're seeing, we have elected to focus on a more mature phase one data readout at a major medical meeting next year in lieu of an R&D day event in December. Our second program, CD38 SADA, recently received IMD clearance from the US FDA to enter clinical development. We're particularly excited about the program given our team's deep CD38 targeted drug development experience. We anticipate exploring potential partnership opportunities as this program advances. The phase one dose escalation, open label single arm multi-center trial, evaluating the safety and tolerability of CD38-SATA in patients with relapsed or refractory non-Hodgkin's lymphoma is anticipated to begin next year. We believe there remains a significant unmet medical need for these patients of both B-cell and T-cell origin, and we look forward to providing further updates as our program advances. In addition, we are continuing to advance multiple preclinical SADA targets and have made encouraging progress, especially on our HER2 and B7H3 constructs. As we look ahead to the rest of 2023 and beyond, we believe we are well positioned with $86.6 million in cash and cash equivalents as of the end of third quarter 2023, which now I believe will extend our cash runway to support our business operations as currently planned into 2027. Of note, our use of cash was only $1.3 million in the third quarter of this year, a direct result of effective capital management strategy and action following our reorganization earlier this year. We believe we have the right strategy in place to drive further Danielle's sales growth, which serves as the financial foundation to propel our SADA technology through clinical development with our two lead programs. We believe we're in a great position to bring forward additional novel therapeutics to cancer patients who need them, while at the same time delivering long-term value to shareholders. I am thrilled to be here at YMAS during this exciting time and look forward to working with this entire team. With that, let me now turn the call over to Sue Smith, who will discuss our U.S. Danielza sales in further detail. Sue?
speaker
Nexidimab
Thank you, Mike, and good morning, everyone. I'm pleased to be with the commercial, to share the commercial progress of Danielza in the U.S. We increased Danielza sales 59% year over year compared to the third quarter of last year. Despite the unevenness from a quarter over quarter standpoint, this is not surprising in rare disease indications. particularly considering the ultra-rare indication of Danielza. We continue to see an upward trend of sales growth since the initial launch back in 2021. Our percent growth since launch is performing well above where Unituxin was at three-year post-launch, 45% versus 22% growth, and we believe we have room for continued growth. As Mike mentioned, we recorded $61 million in Danielza sales in the first nine months of 2023. We expect to meet our full year 2023 sales guidance of between $80 million and $85 million in Danielza sales. Let me review key highlights from Danielza U.S. sales in the third quarter. At the close of the third quarter of 2023, we had a total of 44 new patient starts year to date. This brings the total of new patients start since launch to 158. We continue to grow outside of MSK with non-MSK vials sold representing 63% of all Danielsa demand in the U.S. during the third quarter. With 57 accounts now having used Danielsa around the U.S., we have seen 22 accounts treat two or more patients in the first nine months of this year. We believe physicians are getting more comfortable using Danielza, with 36 healthcare providers having prescribed Danielza in the first nine months of this year, including seven ACPs starting two or more patients in the first nine months of this year. Since launch, a total of 88 doctors have prescribed Danielza, and 28 of them have started treatment on two or more patients as of September 30th, 2023. Our U.S. commercial sales team has received increasingly positive HCP feedback on Danielza through over 2,500 customer interactions in the first nine months of this year and over 6,400 interactions since our launch in 2021. We also continue to see institutional adoption of Danielza, which has been added to five hospital formularies in the first nine months of this year, bringing the total since launch to 41 hospital formularies. YMABS remains a leader in the U.S. anti-GD2 market, a highly important area of pediatric cancer, and a rare disease market with a flat incidence rate. Looking ahead to the fourth quarter of this year and beyond, we are intensifying our market efforts, and our commercial team is in the process of rolling out a brand new Danielsa campaign. The new campaign repositions and elaborates on Danielsa's differentiating characteristics in the treatment of high-risk neuroblastoma, for patients who have experienced incomplete response to induction therapy in their bone and bone marrow. Utilizing our pre-specified interim analysis data, which was consistent with our label, the campaign enables us to share our data for refractory versus relapsed patients separately, providing more detailed data regarding Danielle's performance in patients with an incomplete response to induction therapy. and also patients who are relapsed, which are two different patient groups. In addition, it demonstrates Danielle's response in children after prior anti-GD2 therapy. I am very proud of this team. They have been hard at work in the preparation and rollout of the new campaign, in addition to achieving year-over-year sales growth. We believe we will begin to see meaningful traction from the new campaign starting next year. Let me now pass the call to Steen, who will discuss the latest progress of our SADA platform in further detail.
speaker
Mike
Thank you, Sue, and good morning, everyone. I'm pleased to provide you with an update on our SADA programs, beginning with the DD2 SADA. Our Phase 1 trial evaluates the safety and durability of DD2 SADA in the treatment of DD2-positive solid tumors including small cell lung cancer, sarcomas, and malignant melanoma, got away in March of this year. This phase one dose escalation single arm multicenter safety study has three parts. Part A explores the dose finding of the SADA molecule itself and testing the dose intervals of two to five days between the protein administration and the lutetium DOTA payload. Part B will determine the optimal dose of lutetium dota, and Part C evaluates the safety and initial signs of efficacy using repeat dosing. Dose escalation is based on two patients in cohorts 1 and 2, followed by a modified 3 plus 3 design. And it's important to emphasize that in each cohort, patients will be observed after dosing in a so-called six-week dose-limiting toxicity period or DLT period. Currently, we are still in part A, and the trial is progressing very well. We have dosed five patients in the third quarter, and at present, we have six active sites with three sites expected to be activated during the fourth quarter of this year. We have advanced through the first two cohorts and are now dosing patients in cohort three. We now have more patients receiving the 200-millipede dose of imbutasone doter. I would like to emphasize that we are still in part A of this trial, which is essential to investigate the safety profile of the protein and to determine the optimal timing to administer the radionuclide. We are pleased with what we have seen so far. No patient has experienced any dose-limiting toxicities to date. Furthermore, no patients have experienced any related severe adverse events or serious adverse events. And of note, We can dose SATA protein with no severe or serious pain signals detected. Today, we also can announce that we believe to have demonstrated proof of concept for the DD2 SATA by demonstrating that the SATA molecules can bind to tumors and that the radionuclide targets SATA as visualized on the SPECT CT scans performed. It's important to note that these early data are not complete. and are not necessarily indicative of the full results or ultimate success of the trials of the startup development program. As seen on the next slide, we are in the opinion that the exposure, the blood PK exposure on the patients look as expected. The data include four patients in each of the two treatment groups, so eight patients in total. The patient dose with 0.3 mg per kg protein, represented here in blue, and the patient dose with 1 mg per kg protein, represented here in purple, are comparable and support the dose intervals of 2 to 5 days as being used so far. On the next slide, we for the first time are sharing a SPECT CT scan demonstrating tumor uptake in one patient. This scan was conducted after an imaging dose of 30 milligray only. We are very encouraged by the data observed so far, and based on this, we are investigating the potential clinical expansion of DD2-SATA into pediatric development next year. We are also pleased how our DD2-SATA problem is progressing, and look forward to sharing further clinical updates anticipated next year at a medical meeting of choice. In addition, as Mike mentioned earlier, we are also excited by the FDA clearance of R&D for our CD38 SADA program in not-Hodgkin lymphoma, focusing on both B- and T-cell lymphomas, and expect to dose the first patient in this phase one trial next year. Now with the addition of the CD38 SADA, we have reached the clinical development phase of our SADA platform in both solid and hematological tumors. We do believe in the potential for the novel start-up technology platform to become the targeted radiopharmaceuticals delivery platform of choice in the future, if approved, potentially altering the treatment landscape across a variety of cancers. I will now hand the call over to Bo Kruse, who will review our financials for the third quarter.
speaker
Sue
Thank you, Stine, and good morning, everyone. The Nielsen net product revenues of $61 million for the nine months ended September 30, 2023, represented an increase of 86% from the $32.8 million reported for the nine months ended September 30, 2022. The increase of $28.2 million was primarily driven by an increase in new U.S. patients and an incremental benefit from expanding international revenues. Our Danielson net product revenues of 20 million in the third quarter of 2023 represented a 59% increase compared to the third quarter of 22 and a marginal decline compared to the second quarter of 23 as we saw some unevenness in international revenues after a series of inventory stocking orders from our international partners as reported in recent quarters. During the three and nine months into September 30th, 2023, We recorded half a million of licensed revenue in accordance with our sub-licensing agreement with Adium following the achievement of the marketing authorization for Daniosa in Mexico in September. Now, moving to operating expenses, our IMD expenses decreased by $7.1 million. and 31 million to 15.4 and 40.8 million for the three and nine months ended September 30th, 2023, respectively, compared to the same periods in 22. The net decrease was primarily due to the decrease in spending on deprioritized programs in connection with our restructuring plan announced in January 2023, which resulted in decreased outsourced manufacturing, outsourced research and supplies, clinical trials, and personnel-related costs. The decrease was partially offset by a $4.1 million increase in accrued time-based clinical milestones related to our SADA technology. Selling, general, and administrative expenses decreased by $3.4 million and $16.5 million to 10.2 million and 33.7 million for the three and nine months ended September 30th 2023 respectively compared to the same periods in 2022. The decrease in SCNA for the three months ended September 30th 2023 was primarily driven by cost saving connection with our restructuring plan. The decrease in SCNA for the nine months ended September 30th 2023 was primarily attributable to a $10.9 million charge related to the departure of our former CEO in Q2 2022, and, to a lesser extent, a $2.9 million decrease in commercialization expenses incurred in 2022 in anticipation of a potential Umberto Map launch. Additionally, we recorded a restructuring charge of $1.1 million in SCNA during the nine months ended September 30, 2023, in connection with the restructuring plan. However, personnel-related costs, inclusive of stock-based compensation, actually decreased in the three and nine months ended September 30, 2023, compared to the corresponding period in 2022 due to the impact of the restructuring plan. We reported a net loss for the quarter in the September 30th, 2023 of 7.7 million or 18 cents per share, basic and diluted, compared to a net loss of 27.5 million or 63 cents per share, basic and diluted, for the third quarter in the September 30th, 2022. The improvement in our net loss was primarily driven by the increased revenues and the growth of the Nielsen coupled with decreased operating expenses in the third quarter of 2023. Additionally, we reported a net loss for the nine months into September 30th, 2023 of 20.4 million or 47 cents per share basic and diluted compared to a net loss of 96.7 million or $2.21 per share basic and diluted for the nine months into September 30th, 2022. The decrease in net loss was primarily driven by higher product revenues, lower R&D expenses, and lower SG&A expenses, inclusive of the $10.9 million decrease for the charge related to the departure of the former CEO in Q2 2022. As mentioned earlier, we ended the third quarter of 2023 with cash and cash equivalents of $86.6 million compared to $105.8 million at year end 2022. The decrease was 19.2 million year to date. Importantly, we reduced our quarterly cash use from 4.7 million to 1.3 million, or about 72% during the third quarter of 2023 compared to the second quarter. We continue to demonstrate responsible cash management along with market expansion for Danielsa and we believe we're in position to reduce our projected full year 2023 operating expenses range from 115 to 120 million to 110 to 115 million which together with working capital adjustments leads to a reduction of the total expected cash burn range for the full year 2023 from 40 to 50 million to $27 to $32 million. The consequential impact on our expected cash runway is that we now believe our cash and cash equivalents will sufficiently support our commercial operations and pipeline programs as currently planned into 2027. We continue to expect full-year 2023 Danielsa net product revenues to be in the range of $80 to $85 million. As we noted in prior quarters, the underlying assumptions for this guidance are important to understand. No new partnerships or other new business development income is included in the assumptions. For the purpose of this analysis of runway only, the Danielsa product revenues are assumed to increase by 10% each year from 24 through 26. We indeed hope to see a higher growth rate for Danielsa as we execute our refined commercial strategy and work to deliver new clinical data that could potentially lead to expanded indications and greater physician adoption. In terms of development activities, we have assumed that our prioritized programs will be advanced at our own expense and no new programs are assumed at this point for purposes of the analysis. No further development of the EmbedderMap program has been assumed for the purpose of this estimate, and we have not assumed any equity or debt offerings or borrowings. We believe YMAPS remains well positioned to execute our strategic mission, our priorities, and to support the delivery of multiple milestones. This concludes the financial update, and I'll now turn the call back to Mike.
speaker
Thomas
Thank you for that overview, Bo. Now let's open the line for questions. Operator, do you have any questions?
speaker
Operator
Thank you. We will now be conducting a question and answer session. If you would like to ask a question, please press star 1 on your telephone keypad. A confirmation tone will indicate your line is in the question queue. You may press star 2 if you would like to remove your question from the queue. For participants using speaker equipment, it may be necessary to pick up your handset before pressing the star keys. One moment, please, while we pull for questions. Our first question comes from Alec Stranahan from Bank of America. Please proceed.
speaker
Alec Stranahan
Hey, guys. Thanks for taking our questions. Just a couple from us. First, you know, I think Sue outlined some changes in the commercialization strategy for Danielza. And I know, Mike, you're probably still settling into the role, but any, you know, what would you say is the single biggest lever that you could pull to help drive growth for Danielza? And, you know, how does that compare to the 10% year-over-year growth that Beau outlined? And then I've got a follow-up.
speaker
Courtney
Well, Alex, thank you for your question. I will pass that to Sue. Sue has a robust plan for our expansion of Danielsa and is in the best position to discuss that. Sue?
speaker
Nexidimab
Thanks, Mike. Thanks, Alex, for your question. There are a couple of really important levers that we're able to pull with this campaign. It actually parses out our efficacy data in the patients who are in the frontline partial response to induction. This is consistent with our label, but our current label blended in our relapsed and refractory data together. By our ability to parse out the efficacy, we are able to demonstrate that a patient who has incomplete response to induction still can have a 46% response rate. So that really enabled us to move the conversation earlier in the patient journey. to just after that induction treatment. So we anticipate that as an important growth lever. Currently about half of our sales are actually in the third line treatment setting after relapse. So this is a significant movement and opportunity. And we also are excited because we have new data that shows our benefit after failing prior anti-GD2 therapy. Another important area, when you think of the Enotuxin users, we still have a 31% response rate after prior anti-GD2 therapy, and some of those patients were able, 17%, to go and get a complete response. So those are two really important new pieces of data that have been resonating very well as we talk to customers, and the team is very excited to be rolling out that campaign.
speaker
Alec Stranahan
Okay, great. Thanks for that. Just one follow-up on CD38 SADA. As you've been thinking about pushing this one into the clinic, have there been any lessons learned from GD2 SADA, you know, dosing or, you know, design of the molecule or the clinical study? Thanks.
speaker
Courtney
Yeah, Alex, I appreciate the question on that. I'm going to pass it over to Steve, who can discuss what what we've learned from GD2 as we move forward next year into CD38. Dave?
speaker
Mike
Thank you. I think what we've learned so far, as I also alluded to earlier, is that it's, until now, it has been quite safe to administer the sider program and the sider protein in particular. So we have seen no serious adverse events related to the protein, and we've seen no uh, great, uh, three plus, uh, aversive and related to the protein. And, and I think that is something that we bring into the next program. When we discuss starting dose of the molecules, we also use, of course, our experience with the non-clinical tox package, uh, to bring over to a CD 38 program. And, and we were happy that if they have accepted that program and now we have to have an open mind. So, so I think we are, we are more confident administering the side of protein into humans now than we were before. And as such, we hope to a little bit more quick dose escalation in the first part of that trial.
speaker
Mike
Thank you. Thank you, Steve.
speaker
Thomas
Next question, operator?
speaker
Operator
Our next question comes from Charles Zhu from Guggenheim. Please proceed.
speaker
Charles Zhu
Hey, good morning, everyone, and thanks for taking our questions. And Mike, congratulations on the new role and also very encouraged to see your excitement over the SADA platform. On that note, regarding the GD2 SADA, given your intent now to put out a more substantial data readout, if I heard that correctly, in a 2024 medical meeting as opposed to the year-end R&D day, what quantity as well as types of data could you potentially present? Could we, for example, see things like additional whole body planar images or organ and tumor dosimetry data or how are you thinking about that? Thank you.
speaker
Courtney
Charles, thank you for your question. I'm going to pass this off to Steve to discuss what information potentially will be available and what we expect to be able to present at a medical meeting this coming year. Steve?
speaker
Mike
Thank you. So for the 2024, we still are in the early part of the human dose escalation study. So this is a safety study as discussed prior. But definitely we now already as discussed of those nine patients and we continue enrollment. So we will be able to share both PK data, biodistribution data, as initial also tumor imaging, which we shared the first picture with you today. So, this kind of information will be ready to be shared during the next year.
speaker
Mike
Thank you.
speaker
Charles Zhu
Yeah, and if I could squeeze in one follow-up on that, if you don't mind. So, you know, just looking at some of the, you know, the initial data that you've presented so far on the G2-SATA, maybe something a little bit more granular, but, you know, notice that your PK data appears to be on the injected protein concentration, but, you know, just also how any color you can provide on a radioisotope uptake into the tumor upon, you know, the 200 millicurie administration. Thank you.
speaker
Mike
Thank you, Charles. Steve?
speaker
Mike
This is early days. As I discussed, we have more patients now receiving the 200 millicrete. Most of the tumor uptake and the biodistribution data is collected on the 30 millicrete dosimetry dose, but we also are planning to include scans after the therapeutic dose going forward. So for now, It looks fine. We are still looking for the scalability of the program. We are dose escalated from 0.1 milligram only, so we are still continuing the dose escalation of protein. So I think we need to await more robust protein data before we disclose and discuss the targeting.
speaker
Charles Zhu
Excellent. Thanks for taking the questions and definitely look forward to that readout next year.
speaker
Mike
Very good.
speaker
Charles Zhu
Next question operator.
speaker
Operator
Our next question comes from Bill Muggan from Canaccord Genuity. Please proceed.
speaker
Bill Muggan
Hey, good morning and welcome, Mike. So two questions for me. When you cite the 57 accounts for Danielza, Is that all that have written and currently set up to write Daniela? Or is there sort of a time cut off to weed out any who may be inactive? And then a question on the SADA platform. Looking forward to potentially trying to read through the GD2 targeting to the CD38 targeting. Are there any unique challenges to targeting CD38 versus GD2 that might prevent a seamless read-through from that data? Thank you.
speaker
Courtney
Bill, thank you. I appreciate the question. We'll take the first part of that, and I'll ask Sue to address the accounts that are set up for Daniels.
speaker
Nexidimab
Thanks Bill for the question. Those 57 accounts are set up to use our product. To give you some perspective, in the United States, only 152 accounts have ever used any anti-GD2 therapy. We're well on our way to over a third of those accounts who are using Danielza. And as we mentioned before, we're seeing deeper penetration of those accounts and also the repeat use in 22 accounts with two or more patients. We're also seeing an increase in the tier one accounts. So we're making good headway from a breadth and a depth standpoint.
speaker
Courtney
And Bill, as far as your second question goes on the GD2 versus CD38, I'm going to pass that to Stine, but understanding that our team has a very deep domain knowledge in CD38, which actually makes it very interesting for us moving forward and being able to target the CD38 receptor. So, Stine.
speaker
Mike
Thank you. Yes, there are some differences between the two, because going to the CD38, we are entering the hematological space. And of course, with a two-step procedure, we also need to make sure that we don't have too much bone marrow involvement, which is part of the protocol development, that we have some limits on how much bone marrow involvement the patient can have in order for us not to put radioactivity directly on the progenitor cells. So there is some slight difference in the protocol development and the inclusion-exclusion criteria, but else, Most of those lymphoma patients also have, like the lymph nodes, of course, involved in which we are quite comparable reaching those areas as compared to the solid tumors we see now with DD2. Very good.
speaker
Thomas
Thank you. Thank you for your questions, Bill.
speaker
Courtney
Operator, next question.
speaker
Operator
Our next question comes from Etzer Darot from BMO Capital Markets. Please proceed.
speaker
Etzer Darot
Great. Thanks for taking the question. And Mike, congrats on the role here as CEO. Just one quick question for me, going back to sort of some of the comments in the 10-Q around the interval of dosing of two to five days for GD2-SIDA and where you ultimately think would be sort of an optimal dosing schedule for the technology sort of moving forward as you kind of go through to sort of Part A into potentially the Part B expansion. Thank you.
speaker
Courtney
Thank you for your question, and I will pass that to Steen as he's only joining the work on the targeting.
speaker
Mike
Thank you, Mike. So I think it's too early to say what you could see on the curves I shared with you earlier on this call. There was a slight shift to the right when you went up in the protein concentration. So likely the dose interval will be longer than the two days, depending on how high we can dose up the protein. And this is a safety precaution. So we will have to wait until we see the 3 and 10 milligram dose cohorts to see how the blood PK behaves. And this will also together with the absorption into the tumor, so biodistribution, tumor dosimetry, will dictate the sweet spot where the best relationship between the free drug in the blood and tumor uptake would be found. So for now, at least we can say that we actually were in a good position here in the early part of the trial, but likely they could be longer than two days.
speaker
Etzer Darot
Thank you.
speaker
Mike
Thank you, Arthur. Next question, operator.
speaker
Operator
Our next question comes from Mike Oles from Morgan Stanley. Please proceed.
speaker
Mike Oles
Good morning, and thanks for taking the question. Maybe just a follow-up on the SADA program. You're in the process of advancing the CD38 program, but just curious how you're thinking about advancing some of those earlier programs, such as the HER2 program, and will you be waiting to see more mature data from GD2 potentially before deciding to advance some of those programs? Thanks.
speaker
Courtney
Mike, I appreciate the question. You know, as we start looking at this, we've committed to submitting an IND every year, and we are going to continue to do that and advance some of the early programs on. We're extremely confident in SADA and what it can do and the problems that it actually addresses in the radiopharmaceutical therapeutic market. So we are going to continue to invest in the early programs and look to introduce INDs on an annual basis in order to continue to advance the overall SADA platform.
speaker
Mike
Okay. Great. Thank you. Thank you, Mike. Next question up.
speaker
Operator
Our next question comes from Robert Burns from HC Wainwright. Please proceed.
speaker
Robert Burns
Hey, guys. Congrats on the quarter, and congrats, Mike, on your appointment as CEO. Just two questions, maybe two and a half, I should say, from me. So since the point of the solid bond form is to reduce radiation-associated toxicities and enable greater doses of radiation to be received, I was curious to know whether or at what level of radiation would you start seeing those DLTs and toxicities that would put patients off of therapy if you weren't given the SATA platform, specifically associated with the lutetium? I'm essentially trying to get at what's the incremental dose level you think you could get given a base level radiation without SATA?
speaker
Courtney
Well, yeah, Robert, thank you for the question. As we're looking at these safety studies and moving forward on a new platform on specific targeting, we're going to be able to really work with these to tailor make what that response looks like and also leveling out what some of the patient individual responses look like. I'll pass it to Steve for some additional color. But as we look at these, our primary goal now is to balance the safety and then move into the efficacy as we move forward with the clinical trials.
speaker
Mike
Steve? Thank you, Mike, and I thank you. I have not much more to add to this because what's really important for us now and the potential benefit of the SADA platform is that you administer the radioactive nuclei when the majority of free protein is out of the system. So the whole goal here is to differentiate from the one-step radionuclease out there in order for us to spare normal tissue. And then we will see from there on how much we can add on to the tumor space, and that's the data.
speaker
Robert Burns
Awesome. Thank you. Second follow-up from me. So, you know, when we think about the CD38 SADA, specifically in the multiple myeloma context, what are you viewing as the benchmark there? Are you viewing the benchmark as just what DARS-Lex did, back in the day or are you looking at these new CD38 targeted agents like Medarcafast Alpha and Hexabody CD38 and then are you also enabling prior Darzalex utilization in those patient populations?
speaker
Courtney
Robert, thank you for your question on that and I'll pass it over to Steve for what the plans are for the phase one and as we move forward.
speaker
Mike
So as discussed earlier on this call, we are starting the phase one program in non-Hodgkin lymphoma. So we're actually not dosing multiple myeloma initially. And that's in order for us to quite quickly create the safety benefit of that molecule. And I do agree that there's a lot of competition on the CD38 molecule, but this is predominantly in multiple myeloma space. And I think what we do have here is completely different mode of action. as compared to the competitors. So I'm quite confident we will later go there, but we will initially start the development plan to start the development here in both the D and T cell space in non-Hodgkin lymphoma.
speaker
Mike
Awesome. Thanks, guys. Thank you, Robert.
speaker
Thomas
Operator, are there any other questions?
speaker
Operator
This concludes our question and answer session. I would like to turn the floor back over to Mike Rossi for closing comments.
speaker
Courtney
Thank you, operator, and thank you, everyone, for your participation on today's third quarter earnings call and for your continued interest in YMADS. We believe we're in a strong position as we work to deliver multiple potential value-creating milestones with our novel SADA technology while continuing to drive adoption, growth, and expansion of the Daniela franchise. Let me say it again. I'm thrilled to be part of this special company and look forward to working as one team with a patient-first mindset and our mission to fight cancer.
speaker
Thomas
Thank you everyone and have a great day.
speaker
Operator
This concludes today's teleconference. You may disconnect your lines at this time. Thank you for your participation.
Disclaimer

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